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Hereditary Disease Foundation (HDF) conference 2024 – Day 2

Welcome to Day 2 of the Hereditary Disease Foundation (HDF) conference! The morning was spent listening to an interview between a neurologist and their patient…

Blue skies for Skyhawk: Positive news from Phase 1 trial for SKY-0515

The stormy trial updates that hung over the Huntington’s disease (HD) field in 2021 have certainly parted, making way for the bright and clear forecast…

Buckle in: Gene therapy AMT-130 appears to slow down signs of Huntington’s disease in Phase I/II clinical trial

New data from uniQure, who developed a one-and-done gene therapy for Huntington’s disease (HD) called AMT-130, indicates that the drug is relatively safe and might…

Positive news from Wave Life Sciences SELECT-HD trial

On 25th June 2024, Wave Life Sciences shared the results of their SELECT-HD clinical trial. This trial tested a therapy called WVE-003, designed to only…

Wave Life Sciences Announces Positive Results from Phase 1B/2A SELECT-HD Trial

Great news on the positive results! Read all the details below. Community Letter Press Release

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