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Buckle in: Gene therapy AMT-130 appears to slow down signs of Huntington’s disease in Phase I/II clinical trial
New data from uniQure, who developed a one-and-done gene therapy for Huntington’s disease (HD) called AMT-130, indicates that the drug is relatively safe and might…
Positive news from Wave Life Sciences SELECT-HD trial
On 25th June 2024, Wave Life Sciences shared the results of their SELECT-HD clinical trial. This trial tested a therapy called WVE-003, designed to only…
Wave Life Sciences Announces Positive Results from Phase 1B/2A SELECT-HD Trial
Great news on the positive results! Read all the details below. Community Letter Press Release
No pivot needed for PTC-518
On June 20, 2024, we received an update from PTC Therapeutics about their ongoing trial, PIVOT-HD. PIVOT is testing PTC-518, a small molecule drug, taken…
SURVEYOR opens the door for drugs that treat cognition
Sage Therapeutics released a press statement on June 11th that focuses on the main results of a study called SURVEYOR, aimed at studying cognition (thinking)…