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A Tiny Genetic Tweak Could Delay Symptoms and Activate Cellular Cleanup for Huntington’s Disease
Scientists often use genetics, the study of DNA, to understand the cellular changes that cause disease. By comparing people’s DNA with their symptoms, they can…
Unzipping the Secrets of DNA Repair
Our bodies are experts at looking after our DNA and are continuously monitoring for any damage that needs to be repaired to keep us healthy….
Tooth fairy therapy? Stem cells from teeth tested in a small Huntington’s disease trial
A small study from Brazil tested whether stem cells from human dental pulp, the soft tissue inside teeth, could help people with Huntington’s disease (HD)….
New insights into intermediate CAG repeats: Mapping the expansion continuum
Why do some people with intermediate CAG repeats, a genetic “gray zone” in Huntington’s disease, develop neurological symptoms while others do not? This article covers…
UniQure and FDA No Longer in Alignment on Approval Pathway for AMT-130
In a very brief press release from uniQure on November 3, 2025 we learned that the company is no longer aligned with the FDA on…