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UniQure and FDA No Longer in Alignment on Approval Pathway for AMT-130
November 5, 2025
In a very brief press release from uniQure on November 3, 2025 we learned that the company is no longer aligned with the FDA on…
October 2025: This Month in Huntington’s Disease Research
October 30, 2025
This month brought new revelations across biomarkers, basic science and community gathering. In particular, we saw how DNA-repair targeting strategies are moving into focus, how…
A Map Through Time: Tracking Huntington’s Disease From Birth in the Brain
October 27, 2025
A new study in mouse models reveals how Huntington’s disease (HD) disrupts brain development over time, even long before symptoms appear. Using advanced sequencing tools…
Additional Clarity: What We Know 4 Weeks After the uniQure News
October 23, 2025
The past 4 weeks have been a whirlwind in the Huntington’s disease (HD) community. On September 25th we had an update from uniQure about a…
How Big Is The Huntington’s Disease Iceberg?
October 21, 2025
Huntington’s disease (HD) is caused by repeating C-A-G letters of genetic code that are too long. Everyone who develops HD is born with 36 or…